What is Eltrombopag?

Treatment of aplastic anaemia patients with ATG and Ciclosporin is well-established. Eltrombopag is one of the newer treatments for aplastic anaemia. It works like a normal hormone that the body produces and it is likely that it stimulates the bone marrow stem cell. The complete mechanisms of action in aplastic anaemia are still being determined. Eltrombopag is a tablet taken at home.

I have aplastic anaemia - is Eltrombopag for me?

Currently eltrombopag is not used in first line treatment for patients with severe aplastic anaemia in the UK, and we are awaiting results of the recent RACE trial.

For other patients, it is used when they have not responded to their first or subsequent treatment options.  Your doctor will discuss treatment options with you as to where in the treatment algorithm eltrombopag is advised.  

You can download or order our leaflet here for information on any side effects, likely response rates and how Eltrombopag interacts with certain foods:

Download our eltrombopag leaflet

Order this as a printed leaflet

A huge THANK YOU goes to colleagues at the St James' Hospital Haematology Team, Leeds for their enthusiastic help and expertise in developing the leaflet.